Oral presentation
RNA splicing, Nonsense mediated decay, RNA therapeutics, neurodegenerative disease, CRISPR, gene editing
Public Summary
We are developing a novel genome engineering strategy that targets disease genes most resistant to CRISPR editing: dominant negative diseases caused by repeat expansions, such as Huntington's disease.
Presenter
Carmelle Catamura
Graduate Student
Liana Lareau, University of California, Berkeley
Other Attending Contributors
Liana Lareau
Lab Head
Liana Lareau, University of California, Berkeley